Tawil R, Wagner R K, Hamel I J, Leung G D, Statland M J, Wang H L, Genge A, Sacconi S, Lochmüller H, Reyes-Leiva D, Diaz-Manera J, Alonso-Perez J, Muelas N, Vilchez J J, Pestronk A, Gibson S, Goyal A N, Hayward J L, Johnson N, LoRusso S, Freimer M, Shieh B P, Subramony H S, van Engelen B, Kools J, Leinhard D O, Widholm P, Morabito C, Moxham M C, Cadavid D, Mellion L M, Odueyungbo A, Tracewell G W, Accorsi A, Ronco L, Gould J R, Shoskes J, Rojas L A, Jiang G J, (2024) Safety and efficacy of losmapimod in facioscapulohumeral muscular dystrophy (ReDUX4): a randomised, double-blind, placebo-controlled phase 2b trial, The Lancet Neurology, https://doi.org/10.1016/S1474-4422(24)00073-5
Publication